Enzyme Replacement in Gaucher Disease
AUTOR(ES)
Beutler, Ernest
FONTE
Public Library of Science
RESUMO
The development of enzyme replacement therapy for Gaucher disease was a triumph of translational medicine. What were the key steps in its development? What are the controversies surrounding its use?
ACESSO AO ARTIGO
http://www.pubmedcentral.nih.gov/articlerender.fcgi?artid=529421Documentos Relacionados
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